Doctors realized that a type of genetic
treatment that uses molecules called antisense Oligonucleotides might work for Mila's case.
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To stop the mutated SRSF2 gene from affecting NMD,
the researchers experimented with a technique called antisense oligonucleotide(ASO) therapy.
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These are chemically engineered Oligonucleotides or short segments of RNA, that
can be made to mirror their target genetic material, namely herpes microRNAs.
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Then new Oligonucleotides that bind at several locations to this RNA are added,
and other oligonucelotides that bind at several locations to those Oligonucleotides.
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Experiments have shown that when patient-derived
B cells are treated with CpG Oligonucleotides, it is not just the B cells
that are capable of secreting a particular antibody that are stimulated;